HYPOTHESIS
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doi:10.20944/preprints202306.2167.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
DMD; Dystrophin; gene expression; transcription; mRNA; RNAseq
Online: 29 June 2023 (16:33:49 CEST)
ARTICLE
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doi:10.20944/preprints202306.2000.v1
Subject:
Biology And Life Sciences,
Life Sciences
Keywords:
Gene therapy; AAV; dual vector; DMD; dystrophin; homologous recombination; concatemerization
Online: 29 June 2023 (02:06:05 CEST)
REVIEW
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doi:10.20944/preprints202201.0265.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
CRISPR; gene editing; Duchenne muscular dystrophy (DMD); exon skipping; NHEJ; dystrophin
Online: 18 January 2022 (17:30:37 CET)
ARTICLE
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doi:10.20944/preprints202103.0535.v1
Subject:
Medicine And Pharmacology,
Immunology And Allergy
Keywords:
chemotherapy; cachexia; 5-fluorouracil; skeletal muscle; p38; NF-κB; dystrophin; desmin
Online: 22 March 2021 (13:12:15 CET)
REVIEW
|
doi:10.20944/preprints202003.0048.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
Duchenne muscular dystrophy; CRISPR; animal models; in vivo testing; dystrophin; mutant generation
Online: 4 March 2020 (04:58:48 CET)
REVIEW
|
doi:10.20944/preprints202401.2158.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
Dystrophin; mitochondria; inflammation; reactive oxygen species; glucocorticoids; cardiomyopathy; neuromuscular disease; therapeutic target; treatment; stress response; ATP; respiration; calcium; ion homeostasis
Online: 31 January 2024 (07:21:25 CET)
REVIEW
|
doi:10.20944/preprints201912.0385.v1
Subject:
Medicine And Pharmacology,
Cardiac And Cardiovascular Systems
Keywords:
dilated cardiomyopathy (DCM); hypertrophic cardiomyopathy (HCM); restrictive cardiomyopathy (RCM); arrhythmogenic right ventricular cardiomyopathy (ARVC); left ventricular non-compaction cardiomyopathy (LVNC); Duchenne muscular dystrophy; dystrophin; genome editing; CRISPR/Cas9; Cpf1 (Cas12a)
Online: 29 December 2019 (13:41:48 CET)