ARTICLE
|
doi:10.20944/preprints202311.1585.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
prime editing; CRISPR/Cas9; gene editing; gene therapy; RYR1-related diseases; neuromuscular diseases; RYR1 gene; mutations
Online: 24 November 2023 (08:51:01 CET)