REVIEW
|
doi:10.20944/preprints202409.1590.v1
Subject:
Biology And Life Sciences,
Biology And Biotechnology
Keywords:
viral vectors; viral application; pseudotyping virus; virus envelope; virus envelope chimera; AAV serotype; AAV variant; capsid; AAV; lentivirus; retrovirus; g-deleted rabies virus; HSV
Online: 22 September 2024 (06:35:32 CEST)
REVIEW
|
doi:10.20944/preprints201810.0010.v1
Subject:
Medicine And Pharmacology,
Ophthalmology
Keywords:
Gene therapy, gene editing, CRISPR/Cas9, Cas12a, dual AAV, triple AAV, clinical trials, retina, hereditary retinal dystrophies
Online: 1 October 2018 (13:52:23 CEST)
ARTICLE
|
doi:10.20944/preprints202103.0411.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
HDV; mouse model; AAV; HDAg; Liver damage
Online: 16 March 2021 (10:14:06 CET)
ARTICLE
|
doi:10.20944/preprints202409.0395.v1
Subject:
Biology And Life Sciences,
Life Sciences
Keywords:
DMD; intein; midi-dystrophin; dual-AAV; AlphaFold; structural predicition
Online: 5 September 2024 (08:20:45 CEST)
ARTICLE
|
doi:10.20944/preprints202306.2000.v1
Subject:
Biology And Life Sciences,
Life Sciences
Keywords:
Gene therapy; AAV; dual vector; DMD; dystrophin; homologous recombination; concatemerization
Online: 29 June 2023 (02:06:05 CEST)
REVIEW
|
doi:10.20944/preprints202312.1101.v1
Subject:
Biology And Life Sciences,
Neuroscience And Neurology
Keywords:
AIBP; Glaucoma; Neuroinflammation; Cholesterol; TLR4; Lipid rafts; Mitochondria; Gene therapy; AAV
Online: 14 December 2023 (14:00:38 CET)
ARTICLE
|
doi:10.20944/preprints202201.0173.v1
Subject:
Medicine And Pharmacology,
Neuroscience And Neurology
Keywords:
γ-synuclein; AAV vector; antisense oligonucleotide; cognitive dysfunction; dopamine; motor deficits
Online: 12 January 2022 (14:27:18 CET)
REVIEW
|
doi:10.20944/preprints202312.1823.v1
Subject:
Biology And Life Sciences,
Aging
Keywords:
aging; senolytic; senescent cells; AAV; anti-aging therapy; cell therapy; gene therapy
Online: 25 December 2023 (16:20:43 CET)
REVIEW
|
doi:10.20944/preprints202012.0602.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
Gene therapy; ocular neovascularization; viral vectors; preclinical; clinical trials; anti-angiogenesis; AAV
Online: 23 December 2020 (17:45:44 CET)
CONCEPT PAPER
|
doi:10.20944/preprints202404.1620.v3
Subject:
Biology And Life Sciences,
Biology And Biotechnology
Keywords:
microglial replacement; adeno-associated viral (AAV) vectors; COURIER; SPIT; base editing; prime editing
Online: 24 May 2024 (11:34:33 CEST)
COMMUNICATION
|
doi:10.20944/preprints202104.0273.v1
Subject:
Medicine And Pharmacology,
Immunology And Allergy
Keywords:
Dry-AMD; oxidative stress; MnSOD; RPE; retinal degeneration; Erythropoietin; gene therapy; Animal model; AAV; ERG
Online: 12 April 2021 (09:37:18 CEST)
HYPOTHESIS
|
doi:10.20944/preprints202404.1631.v2
Subject:
Biology And Life Sciences,
Biology And Biotechnology
Keywords:
encapsulation; adeno-associated virus (AAV); light-activated allosteric protein switch; Deadman switch; T4 bacteriophage gene delivery vector; facultative intracellular bacteria
Online: 26 April 2024 (14:49:58 CEST)
REVIEW
|
doi:10.20944/preprints202310.0414.v1
Subject:
Medicine And Pharmacology,
Neuroscience And Neurology
Keywords:
primate evolution genetics; noncoding genome; immunogenetics; neurogenetics; neurobiology; cell biology; molecular biology; neurological diseases; cardiovascular diseases; brain-immune system interactions; nucleic acid therapeutics; RNA interference; AAV vectors; blood-brain-barrier
Online: 8 October 2023 (07:20:59 CEST)