REVIEW
|
doi:10.20944/preprints202212.0022.v1
Subject:
Medicine And Pharmacology,
Pharmacology And Toxicology
Keywords:
Fabry disease; globotriaosylceramide; α-galactosidase-A; enzyme replacement therapy; chaperone therapy; migalastat
Online: 1 December 2022 (09:50:49 CET)