REVIEW
|
doi:10.20944/preprints201910.0365.v1
Subject:
Medicine And Pharmacology,
Pharmacology And Toxicology
Keywords:
pharmacological chaperones; mucopolysaccharidoses; mps; small molecules
Online: 31 October 2019 (09:33:43 CET)
ARTICLE
|
doi:10.20944/preprints202305.2104.v1
Subject:
Biology And Life Sciences,
Immunology And Microbiology
Keywords:
Lysosomal storage diseases; Mucopolysaccharidoses; Glycosaminoglycans; Leukocytes; Lymphocytes
Online: 30 May 2023 (10:01:40 CEST)
REVIEW
|
doi:10.20944/preprints202303.0552.v1
Subject:
Medicine And Pharmacology,
Neuroscience And Neurology
Keywords:
Mucopolysaccharidoses; Disease Modeling; in vitro models; induced Pluripotent Stem Cells (iPSCs); Dental Pulp Stem Cells (DPSC)
Online: 31 March 2023 (14:43:34 CEST)